UniQure stock crashed Monday on "confusing" and "unexpected" feedback from the FDA for its Huntington's disease gene therapy.

Pivotal results from uniQure’s gene therapy for Huntington’s disease have brought new light to patients who have known only ...

The United States Huntington's Disease Treatment Market is set to expand significantly, with an expected CAGR of 15.22% from ...

This image shows three brain cells with the faulty protein that causes Huntington’s disease. The bright yellow cell in the middle has built up a clump of this protein inside it. The blue spots in the ...

Huntington’s disease is a genetic disorder that is caused by an unusual number of repeats in the huntingtin gene; there make the gene too long, and lead to the production of a toxic protein in brain ...

More than 2 out of 5 adults in the U.S. are considered obese, according to the Centers for Disease Control and Prevention. But what if there was a way to test children to find out if they’re at higher ...

Figuring out how many people have 36 or more CAG repeats, but never show up to a doctor, is a bit like an iceberg. There’s a ...

When it came time to start a family, Sarah Elizabeth Orlando, 33, knew she would go about it differently. Before she was born, an in-utero amniocentesis had confirmed she carried the gene for fragile ...